CRISPR gene therapy Casgevy can nearly eliminate sickle cell crises, but difficult stem‑cell collection is delaying access ...
For most of his 20 years, a New Jersey man knew pain as a daily reality. Now, after a one-time CRISPR gene-editing treatment at Children's Hospital of Philadelphia, Austin Louis says he is finally ...
A high dose of sickle cell drug pociredir boosted fetal hemoglobin and reduced red blood cell destruction in adults with ...
Because the sickle cell gene mutation is believed to have evolved as a protection against malaria, a deadly parasitic infection spread by mosquitos, most common in Africa and Asia, Black people are at ...
As Uganda rolls out mandatory nationwide screening of newborns for sickle cell disease this month, a gene therapy celebrated ...
It took a while for the science to basically catch up to that suspicion.” In these types of “recessive” conditions, the ...
In Ghana newborn screening for sickle cell disease is rare, with many children going undiagnosed until painful symptoms force emergency care. The International Sickle Cell Centre (ISCC), a nonprofit ...