The U.S. Social Security Administration has requested that the National Academies of Sciences, Engineering, and Medicine conduct a study to (1) provide an overview of ways to collect information about ...
Jessica Nance, MD, MS, discusses the significance of surrogate end points, like functional assessments, in clinical trials of treatments for Duchenne muscular dystrophy and their implications for ...
The evolution of functional assessments for spinal muscular atrophy (SMA) highlights the challenges of adapting pediatric scales for adults and the need for modified evaluations to accurately measure ...
Some results have been hidden because they may be inaccessible to you
Show inaccessible results
Feedback